Risdiplam

Risdiplam

Risdiplam

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0 Metric Ton

Negotiable

  • Min.Order :0 Metric Ton
  • Purity: 98%

Keywords

Risdiplam 98% 1825352-65-5

Quick Details

  • Appearance:yellow solid
  • Application:Risdiplam, also known as RG7916 and RO7034067, is a gene splicing modulator (neuromuscular disease).
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  • ProductionCapacity:|Metric Ton|Day
  • Storage:rt
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Superiority:

Risdiplam is a modifier of SMN2 splicing, leading to an increase in SMN2 full-length transcript and thus functional SMN protein. Risdiplam modulates SMN2 pre-mRNA splicing towards the production of full-length SMN2 mRNA and increases SMN protein levels [1].

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